NatureCorrecting congenital myasthenia-associated acetylcholine receptor defectsHuanhuan LiNuriya MukhtasimovaJinfeng TengElfie S. CavalliXilin GuJason K. SelloSteven M. SineRyan E. Hibbs2026-07-01Full textDOI https://doi.org/10.1038/s41586-026-10706-1