DG9 boosts PMO nuclear uptake and exon skipping to restore dystrophic muscle and cardiac function
- Md Nur Ahad Shah
- Harry Wilton-Clark
- Farhia Haque
- Brooklynn Powell
- Laura Edellein Sutanto
- Radha Maradiya
- Pavel Zhabyeyev
- Rohini Roy Roshmi
- Saeed Anwar
- Tejal Aslesh
- Kenji Rowel Q. Lim
- Rika Maruyama
- Anne Bigot
- Courtney S. Young
- Scott Bittner
- Melissa J. Spencer
- Hong M. Moulton
- Gavin Y. Oudit
- Toshifumi Yokota
2025-05-14