Gmppb-mutant mice exhibit dystroglycanopathy symptoms that are rescued with GSK3β inhibition or AAV-mediated GMPPB gene replacement
- Ziwei Fu
- Tongchao Wang
- Chenyang Zhang
- Tianyu Qi
- Yanyan Chen
- Ju Yang
- Hua Yang
- Bing Yan
- Baoming Gong
- Weiqiao Lu
- Sushan Luo
- Ying Liu
- Lei Sun
- Hao Jiang
- Bo Chen
- Zhao Zhang
- Xiuping Liu
- Yuxiang Wang
2026-04-09