Nature CommunicationsMorpholino–RNA duplex exhibits robust, sustained, and safe steric-block antisense activity by intracerebroventricular and intrathecal injectionMitsugu YanagidairaTetsuya NagataJuri HasegawaTakashi IshiiSatoe EbiharaMakiko NawaTakanori Yokota2025-12-22Full textDOI https://doi.org/10.1038/s41467-025-66765-x