Leonard Petrucelli2 articles listing Leonard Petrucelli in PNAS, Science, indexed by Paperzzz from Crossref and OSF.Blocking RAN translation without altering repeat RNAs rescues C9ORF72 -related ALS and FTD phenotypes ScienceCryptic intronic transcriptional initiation generates efficient endogenous mRNA templates for C9orf72-associated RAN translation PNAS