Leonard Petrucelli

2 articles listing Leonard Petrucelli in PNAS, Science, indexed by Paperzzz from Crossref and OSF.

  1. Blocking RAN translation without altering repeat RNAs rescues C9ORF72 -related ALS and FTD phenotypes Science
  2. Cryptic intronic transcriptional initiation generates efficient endogenous mRNA templates for C9orf72-associated RAN translation PNAS